1068 correction of the hematopoietic phenotype of fanconi anemia a knockout mice using retroviral vectors encoding the human FANCA cDNA

1068 Correction of the Hematopoietic Phenotype of Fanconi Anemia A Knockout Mice Using Retroviral Vectors Encoding the Human FANCA cDNA Molecular Therapy Vol 5, No 5, May 2002, Part 2 of 2 Parts Copyr[.]

Molecular Therapy Vol 5, No 5, May 2002, Part 2 of 2 Parts Copyright © The American Society of Gene Therapy

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1066 Effect of Ultraviolet B Irradiation on Chimeric

RNA-DNA Oligonucleotide Induced Gene Correction

Li-Wen Lai,1 Orlantha Whitehair,1 Paula D Campbell,1 Yeong-Hau H

Lien.1

1 Medicine, University of Arizona, Tucson, AZ, United States

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1067

1067 Adenovirus T Adenovirus T Adenovirus Transduction Promotes the ransduction Promotes the Expression of Multiple Chemokines in βββββ-TC3 Cells and -TC3 Cells and Murine Pancreatic Islets

Nan Zhang,1,2 Bernd Schröppel,3 Barbara Murphy,2,3 Jonathan S Bromberg,1,2 Randall S Sung.2

1 Carl C Icahn Institute of Gene Therapy and Molecular Medicine, Mount Sinai School of Medicine, New York, New York, United States; 2 Recanati-Miller Transplantation Institute, Mount Sinai School of Medicine, New York, New York, United States; 3 Division

of Nephrology, Department of Medicine, Mount Sinai School of Medicine, New York, New York, United States

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1068 Correction of the Hematopoietic Phenotype of Fanconi Anemia A Knockout Mice Using Retroviral V

Vectors Encoding the Human ectors Encoding the Human F FANCA ANCA ANCA cDNA cDNA

Jose C Segovia,1 Paula Rio,1 Helmut Hennenberg,2 Jose A Casado,1 Jesus Martinez,1 K Göttsche,2 N C Cheng,3 H J Van de Vrugt,3 F Arwert,3 Hans Joenje,3 Juan A Bueren.1

1 Hematopoiesis, CIEMAT, Madrid, Spain; 2 Klinik fŸr Pädiatrische Hämatologie und Onkologie, Z fŸr Kinderheilkunde, Heinrich-Heine-Universität, DŸsseldorf, Germany; 3 Clinical Genetics and Human Genetics, Free University Medical Center, Amsterdam, Netherlands

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1069 Real-Time PCR SYBR Green Genotype Assay for

a Murine Knock-Out Model of Mucopolysaccharidosis

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Type I ype I

Michelle C Rickard,1 Beth E Larson,1 Chester B Whitley.1

1 Gene Therapy Center - Pediatrics - Institute of Human Genetics,

University of Minnesota, Minneapolis, Minnesota, United States

1070 Gene T

1070 Gene Transfer into Human Hematopoietic Stem ransfer into Human Hematopoietic Stem Cells Application to the Gene Therapy of Congenital Erythropoietic Porphyria

Fabien Geronimi,1 Isabelle Lamrissi-Garcia,1 Emmanuel Richard,1

François Moreau-Gaudry,1 Miquel Morey,2 Hubert de Verneuil.1

1 Laboratoire PMTG, INSERM EMI 0211, Université Victor Ségalen Bordeaux 2, Bordeaux, France; 2 Servicio de Hematologia y Hemoterapia, Hospital Son Dureta, Palma de Mallorca, Spain

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1071 Highly Efficient Lentiviral V

1071 Highly Efficient Lentiviral Vector-Mediated ector-Mediated T

Transduction of Uncultured, Nondividing and Fully Re- ransduction of Uncultured, Nondividing and Fully Re-Implantable Primary Hepatocytes

T H Nguyen,1 J Oberholzer,2 J Birraux,3 P Majno,2 D Mattey,2 S Vianin,1 P Morel,2 D Trono.1

1 Department of Genetics and Microbiology; 2 Department of Surgery; 3 Department of Pediatrics, University of Geneva Medical school, Geneva, Switzerland

Vectors Encoding the Human ectors Encoding the Human F FANCA ANCA ANCA cDNA< /b> cDNA< /b>

Jose C Segovia,1 Paula Rio,1... Sinai School of Medicine, New York, New York, United States

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1068 Correction of the Hematopoietic Phenotype of Fanconi Anemia A Knockout Mice Using Retroviral. .. Bordeaux 2, Bordeaux, France; 2 Servicio de Hematologia y Hemoterapia, Hospital Son Dureta, Palma de Mallorca, Spain

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